Global Medical Affairs Director Rare Diseases

Are you ready to lead and innovate in a dynamic, patient-focused biopharmaceutical company?

Ipsen is a growing global specialty-driven biopharmaceutical company focused on innovation and specialty care. We aim to make a sustainable difference by significantly improving patients' health and quality of life, providing effective therapeutic solutions for unmet medical needs through differentiated and innovative medicines in Oncology, Neurosciences, and Rare Diseases.

As Medical Director in Rare Diseases, you will lead the design and execution of the global medical strategy for highly specialized assets with significant unmet medical need.

Reporting to the Medical Asset Lead, you will play a key role in shaping the clinical and scientific narrative, enabling evidence generation, and building trusted partnerships with the rare disease community.

Your work will directly inform strategic decision-making and ensure patient-centric approaches across the product lifecycle.

Global Medical Affairs Director Rare Diseases

Ipsen is a mid-sized global biopharmaceutical company with a focus on transformative medicines in three therapeutic areas: Oncology, Rare Disease and Neuroscience. Supported by nearly 100 years of development experience, with global hubs in the U.S., France and the U.K, we tackle areas of high unmet medical need through research and innovation.

Our passionate teams in more than 40 countries are focused on what matters and endeavor every day to bring medicines to patients in 88 countries. We build a workplace that champions human-centric leadership and fosters a culture of collaboration, excellence and impact. At Ipsen, every individual is empowered to be their true selves, grow and thrive alongside the company's success. Join us on our journey towards sustainable growth, creating real impact on patients and society!

For more information, visit us at https://www.ipsen.com/ and follow our latest news on LinkedIn and Instagram.

• Patient-Focused: The patient is at the heart of everything we do, and improving their outcomes is the deliverable of every strategy.
• Employee Care: We care for our employees, who are the ambassadors making a real difference.
• Bold Leadership: We attract and develop bold, agile, entrepreneurial individuals who take full ownership of their decisions.
• Growth Opportunities: We offer a wealth of fulfilling challenges and growth opportunities in a fast-moving, game-changing organization.

• Lead the development and implementation of the Global Medical Plan for assigned rare disease assets, integrating
• the evidence generation plan, thought leader (TL) engagement strategy, and medical communications roadmap.
• Serve as a core member of the cross-functional asset team, aligning medical priorities with clinical development, regulatory, commercial, and market access strategies.
• Contribute to indication-specific medical budget planning and ensure efficient allocation of resources in line with strategic objectives.

• Drive the design and execution of global and international clinical studies and real-world evidence (RWE) programs, tailored to the unique challenges of rare disease populations
• Support affiliate-led studies by providing strategic and scientific input, reviewing protocols, and guiding execution to ensure consistency with global priorities.
• Ensure full compliance with GCP, ethical standards, and internal medical governance; establish fit-for-purpose oversight mechanisms for all data-generating activities.

• Develop and sustain collaborative relationships with global and local key opinion leaders, patient advocacy groups, and academic centers of excellence.
• Represent the company at international congresses, scientific symposia, advisory boards, and high-level stakeholder engagements, contributing as a respected medical voice in rare disease discourse.
• Partner with external stakeholders to identify opportunities for research collaborations, policy shaping, and medical education aligned with the Global Medical Affairs strategy.

• Act as the rare disease medical expert within the organization, providing strategic and scientific input across functions and geographies.
• Independently lead high-impact initiatives that address key scientific, clinical, or strategic challenges within your asset scope.
• Contribute to shaping the long-term vision for rare disease assets, from early development through launch and postapproval stages.